Pre-Conference Workshop Day

10:00 - 12:00

WORKSHOP A: Innovative Approaches to Data Dissemination that Amplify the Value Story

This workshop sets out to explore how to create a meaningful value story around your gene therapy, discover here:

  • Novel approaches and formats being adopted to amplify the value story externally
  • Value associated with different communications strategies such as congresses and publications
  • Best data dissemination strategy to support a successful launch

Workshop Leaders:

REW Pardot speaker photos (7)
REW Pardot speaker photos (8)

Alexis Russell
Senior Director,
US Gene Therapy Therapeutic Area Lead
PTC Therapeutics

Ramin Farhood
Vice President of Medical Affairs
SSI Strategy

14:00 - 16:00

WORKSHOP B: Approaches to Support the Critical Need for Post Marketing Surveillance in Gene Therapy

This workshop sets out to discuss the mechanisms being used to collect longterm data on safety, variability and durability of efficacy of gene therapies. Learn how to:

  • Review the regulatory elements of post marketing surveillance
  • Adopt an approach to collecting additional data that supports the understanding of gene therapy outcomes and their impact on the lives of patients with rare diseases

Workshop Leaders:

REW Pardot speaker photos (9)

Ian Winburn
Vice President, Global Medical Team Lead, Haemophilia, Endocrine In-Born Errors of Metabolism and Transplantation